Rationally engineered Cas9 nucleases with improved specificity

Slaymaker et al. (2016). Science DOI: 10.1126/science.aad5227 Citations: 3055

Key findings

Developed enhanced-specificity Cas9 (eSpCas9) through charge neutralization in non-target strand binding groove. Reduced off-targets while preserving on-target activity. Complementary approach to HF1.

Parts used