AAVmyo3 Serotype

Third AAVmyo variant completing the muscle-targeted capsid shuffling series with distinct muscle tropism.

Length: 1 bp

Tropism: Skeletal muscle, limb muscles, cardiac muscle (moderate)

Characteristics

Alternative muscle tropism profile. Balanced skeletal muscle coverage. Moderate cardiac transduction. Reduced hepatic uptake.

Applications

Multi-muscle tissue disorders. Systemic muscular dystrophy gene therapy. Alternative to AAVmyo and AAVmyo2.