Targeted nucleotide editing using hybrid prokaryotic and vertebrate adaptive immune systems

Nishida et al. (2016). Science | DOI: 10.1126/science.aaf8729 | Citations: 1761

Key Finding

Alternative cytosine base editor using sea lamprey PmCDA1 cytidine deaminase fused to Cas9 nickase. Target-AID modifies 3-5 base window 18 bases upstream of PAM with greatly reduced toxicity versus nuclease-based CRISPR systems.

Parts Used