Improving cytidine and adenine base editors by expression optimization and ancestral reconstruction

Koblan et al. (2018). Nat Biotechnol | DOI: 10.1038/nbt.4172 | Citations: 1090

Key Finding

Codon optimization and enhanced nuclear localization signals generated BE4max with 1.8-fold higher editing versus BE4. Ancestral reconstruction of APOBEC1 (Anc689 with 36 substitutions) created AncBE4max showing 1.7-9× improvement depending on plasmid dose.

Parts Used